We reported previously about the pharmaceutical company Takeda having an interest in ataxia and them developing a drug that targets the cerebellum. It is really encouraging to see that this work has now progressed to the human trial stage, and a trial has started testing the effect of their drug, called Tak-831, in people with Friedreich’s ataxia.
This is a placebo-controlled trial in 65 people with FA for 12 weeks and their main aim is to test the effect on the function of the arms and hands and manual dexterity (using the 9-hole peg test). They will also test a number of other measures.
Ataxia UK has been actively supporting Takeda by providing advice, information on the patient perspective and introductions. We are hoping to hold a meeting of European patient groups soon to assist in the advancement of the programme. You can read more about the trial here.
Posted on 11/07/2018