Chondrial Therapeutics Announces Dosing of First Patients in Phase 1 FA trial – Ataxia

Chondrial Therapeutics Announces Dosing of First Patients in Phase 1 FA trial

Chondrial Therapeutics Announces Dosing of First Patients in Phase 1 FA trial

Chondrial Therapeutics is a biotechnology company focused on developing treatments for Friedreich’s ataxia (FA). They recently announced that the first person has been treated in a Phase 1 clinical trial to assess the safety and tolerability of CTI-1601. People with FA have reduced amounts of protein called frataxin in their cells. CTI-1601 is a treatment that aims to deliver the frataxin protein to the cells of people with FA, and therefore treat the underlying cause of the condition.

Carol Ben-Maimon, MS, President and Chief Executive Officer of Chondrial Therapeutics said “CTI-1601 is designed to address the root cause of Friedreich’s ataxia – low levels of frataxin. The initiation of our Phase 1 clinical program was supported by positive preclinical data and is an important step forward for patients affected by FA, a devastating and progressive disease for which there is no cure”.

The trial is taking place in the US, and results are expected by the end of 2020. Read the full press release here.

Posted on 19/12/2019

SUBSCRIBE TO OUR NEWSLETTER

Something went wrong. Please check your entries and try again.
fundraise image

FUNDRAISE FOR US

Take part in a challenge or create your fundraiser. Every penny you raise will help those affected by ataxia.

Donate Image

DONATE

To make either a one off or recurring donation which will help fund research into treatments and cures and supports those affected ataxia

Volunteer Image

VOLUNTEER WITH US

Support the ataxia community and volunteer with Ataxia UK. From social media to telephone befriending, there are loads of ways you can make a difference to someone's life.

Donate Now
Welcome to our new site! We hope you like it.
As it's brand new, there may be a few temporary glitches such as broken links - we are working on getting these all fixed ASAP. If you'd like to give us any feedback or let us know if something isn't quite right, please email website@ataxia.org.uk
+
Scroll to Top