New EU Orphan drug designation for Freidreich’s ataxia
Omaveloxolone has recently been given an Orphan drug designation for Friedreich’s ataxia the European Medicines Agency.
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Friedreich’s ataxia
Hope for gene therapy for Friedreich’s ataxia
This week results were published showing the effects of an AAV (adeno-associated virus) gene therapy in a new mouse model of Friedreich’s ataxia (FA).
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Results of a study evaluating TAK-831 in adults with Friedreich’s ataxia (FA)Â
A new placebo-controlled trail in humans, testing a novel therapy, Tak-831 for Friedreich’s ataxia, has begun in America.
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Increasing levels of a protein in FA may be potential future therapy
Experiments performed in mice and in cells taken from Friedreich’s ataxia (FA) patients reveal a protein called ‘GRP75’ might be an effective future treatment approach.
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Data released from preclinical study into gene therapy for Friedreich’s ataxia
The latest findings from a trial testing a potential new gene therapy for Friedreich’s ataxia have been announced.
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Research News – May and June 2018
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Research News – October and November 2017
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Research study aiming to improve speech in Friedreich’s ataxia looking for participants
A speech therapy clinical trial aiming to begin in February are urgently seeking people with FA to take part.
Research News – August and September 2017
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Latest Research News – March and April 2017
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Latest Research News – January and February 2017
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Latest Research News – December 2016
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Latest Research News – September and October 2016
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Latest Research News – July and August 2016
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Latest research news – May and June 2016
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